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Project CASK Commits $250,000 to Small Molecule Treatment Research for CASK Gene Disorders
Project CASK committed $250,000 to a cross-institutional collaboration between Dr. Hans-Jurgen Kreienkamp at UKE Hamburg and Dr. ChangHui Pak at UMass Amherst. Their study targets the CASK-Liprin-alpha interaction in pontocerebellar hypoplasia, testing a compound that may halt cerebellar cell death. A second major therapeutic avenue alongside gene therapy.

Hitomi Kubo
Aug 31, 20242 min read
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